Intellia Therapeutics said its Crispr-based treatment for hereditary angioedema met its goals in a Phase 3 trial, marking a ...

As cell and gene therapy leaders gathered in Maryland to discuss accelerating clinical trials in children, one “cutting edge” ...

Mayo Clinic's Engineering & Therapeutics in Gastrointestinal Disease Lab is developing new ways to deliver gene therapy into organs through endoscopic procedures endoscopists already perform.

Paterna Biosciences said it has mastered the molecular signals that teach stem cells how to mature into sperm for a promising ...

Program to expand access to exome sequencing to help clinicians confirm diagnosis and guide clinical decision-making in NPC GAITHERSBURG, Md.--(BUSINESS WIRE)-- GeneDx (Nasdaq: WGS), the leader in ...

Program to expand access to exome sequencing to help clinicians confirm diagnosis and guide clinical decision-making in NPC GeneDx (Nasdaq: WGS), the leader in rare disease diagnosis and improving ...

Scientists have uncovered a powerful genetic switch that helps some of the body’s most important immune cells grow up properly and keep our organs healthy. The switch, called MafB, guides immature ...

Last week, the California Institute for Regenerative Medicine (CIRM) approved a new funding program aimed at accelerating gene therapies for rare diseases by moving away from traditional approaches ...

Amid news of the splashy $4.8 billion Amicus buy, BioMarin has slipped in the discontinuation of a genetic liver disease candidate it had once hoped would become a best-in-class treatment. The oral ...

NEW YORK CITY (WABC) -- New York City is launching a groundbreaking program to prevent sudden deaths. The city's medical examiner will offer free genetic screening to at-risk family members of people ...

When roundworms stop reproducing, they can still move and function normally but lose their ability to detect certain food odors that once led them to their meals. Researchers at Nagoya University have ...

Gift Article 10 Remaining As a subscriber, you have 10 articles to gift each month. Gifting allows recipients to access the article for free. Chicago philanthropists Don and Anne Edwards have donated ...